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Clinical Features of Families with a Novel Pathogenic Mutation in Sepiapterin Reductase

  • Feda E. Mohamed
  • , Lara Alzyoud
  • , Mohammad A. Ghattas
  • , Mohammed Tabouni
  • , André Fienemann
  • , Joanne Trinh
  • , Ibrahim Baydoun
  • , Praseetha Kizhakkedath
  • , Hiba Alblooshi
  • , Qudsia Shaukat
  • , Rim Amouri
  • , Matthew J. Farrer
  • , Samia Ben Sassi
  • , Fatma Al-Jasmi

Research output: Contribution to journalArticlepeer-review

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Biochemistry, Genetics and Molecular Biology